SPLICING
SCIENTISTS CREATE NOVEL RNA REPAIR TECHNOLOGY and SCIENTISTS CREATE POTENT MOLECULES AIMED AT TREATING MUSCULAR DYSTROPHY
Modeling Childhood-onset Myotonic Dystrophy Jordan Gladman Ph.D. PRPR 9/24/2012.
1 Effects of IPLEX in Myotonic Dystrophy Type 1 (DM1) Muscle Study Group Annual Meeting 9/16/2008, Beaver Hollow, NY Richard T. Moxley, III, MD.
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Nemoci spojené s expanzí mikrosatelitních repetitivních sekvencí – myotonická dystrofie typu 1 Kongenitální myotonie a mutace v genu CLCN1.
Myotonia Congenita Shannon L Venance, MD PhD ICNDM, Kansas City June 3, 2007.
Modeling Childhood-onset Myotonic Dystrophy